Arimoclomol as a potential therapy for neuronopathic Gaucher Disease
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B. Bembi | T. Kirkegaard | A. Dardis | P. Peruzzo | Nikolaj H. T. Petersen | P. Zago | R. Magnoni | E. Malini | Lukasz M. Solanko | C. Bornaes | Cathrine Kolster Fog-Tonnesen