论文信息 - A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II - 字舞流文

A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II

M. Mascelli | C. Hendriksz | Zheng Fan | S. Santra | J. Muenzer | Luying Pan | K. Sciarappa | A. Barbier | G. Solanki | S. Vijayaraghavan | V. Perry | Nan Wang