Oral Migalastat HCl Leads to Greater Systemic Exposure and Tissue Levels of Active α-Galactosidase A in Fabry Patients when Co-Administered with Infused Agalsidase
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D. Lockhart | J. Flanagan | C. Barlow | D. Warnock | F. Eyskens | D. Bichet | O. Goker-Alpan | F. Johnson | K. Nicholls | S. Sitaraman | B. Wustman | R. Khanna | S. Shankar | M. Holida | Mark Thomas | P. Boudes | K. Valenzano | J. Barth | Mathews Adera