Long-term efficacy and safety of inotersen for hereditary transthyretin amyloidosis: NEURO-TTR open-label extension 3-year update
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M. Benson | P. Dyck | M. Gertz | G. Merlini | I. Conceição | A. Mazzeo | M. Polydefkis | A. Narayana | V. Planté-Bordeneuve | A. Kristen | J. Berk | T. Brannagan | L. Obici | C. Whelan | B. Drachman | J. Gámez | P. Gorevic | T. Coelho | L. Gentile | J. M. Plana | Annabel K. Wang | K. Olugemo | P. Aquino
[1] C. Karam,et al. Early Data on Long-term Impact of Inotersen on Quality-of-Life in Patients with Hereditary Transthyretin Amyloidosis Polyneuropathy: Open-Label Extension of NEURO-TTR , 2021, Neurology and Therapy.
[2] M. Kosinski,et al. Responder analysis for neuropathic impairment and quality-of-life assessment in patients with hereditary transthyretin amyloidosis with polyneuropathy in the NEURO-TTR study , 2021, Journal of Neurology.
[3] C. Karam,et al. Rate of neuropathic progression in hereditary transthyretin amyloidosis with polyneuropathy and other peripheral neuropathies: a systematic review and meta-analysis , 2021, BMC Neurology.
[4] D. Pareyson,et al. Hereditary transthyretin amyloidosis overview , 2020, Neurological Sciences.
[5] J. Healey,et al. What Are the Minimum Clinically Important Differences in SF-36 Scores in Patients with Orthopaedic Oncologic Conditions? , 2020, Clinical orthopaedics and related research.
[6] F. Salvi,et al. Early data on long‐term efficacy and safety of inotersen in patients with hereditary transthyretin amyloidosis: a 2‐year update from the open‐label extension of the NEURO‐TTR trial , 2020, European journal of neurology.
[7] M. de Carvalho,et al. Health-related quality of life in hereditary transthyretin amyloidosis polyneuropathy: a prospective, observational study , 2020, Orphanet Journal of Rare Diseases.
[8] P. Hawkins,et al. Expert consensus recommendations to improve diagnosis of ATTR amyloidosis with polyneuropathy , 2020, Journal of Neurology.
[9] M. Gertz,et al. Advances in the treatment of hereditary transthyretin amyloidosis: A review , 2019, Brain and behavior.
[10] M. Kürtüncü,et al. Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis , 2019, Turkish Journal Of Neurology.
[11] M. Fehlings,et al. Minimum Clinically Important Difference in SF-36 Scores for Use in Degenerative Cervical Myelopathy , 2018, Spine.
[12] W. Lenderking,et al. Characterizing the High Disease Burden of Transthyretin Amyloidosis for Patients and Caregivers , 2018, Neurology and Therapy.
[13] D. Adams,et al. Familial amyloid polyneuropathy , 2017, Current opinion in neurology.
[14] M. Gertz. Hereditary ATTR amyloidosis: burden of illness and diagnostic challenges. , 2017, The American journal of managed care.
[15] T. Tripp,et al. Clinical measures in transthyretin familial amyloid polyneuropathy , 2017, Muscle & nerve.
[16] Sanjiv J. Shah,et al. Genotype and Phenotype of Transthyretin Cardiac Amyloidosis: THAOS (Transthyretin Amyloid Outcome Survey). , 2016, Journal of the American College of Cardiology.
[17] B. Hazenberg,et al. First European consensus for diagnosis, management, and treatment of transthyretin familial amyloid polyneuropathy , 2016, Current opinion in neurology.
[18] M. Benson,et al. Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis. , 2015, Journal of the American College of Cardiology.
[19] P. Hawkins,et al. Quality of life in ATTR amyloidosis , 2015, Orphanet Journal of Rare Diseases.
[20] O. Karayal,et al. THAOS: Gastrointestinal manifestations of transthyretin amyloidosis - common complications of a rare disease , 2014, Orphanet Journal of Rare Diseases.
[21] B. Roitberg,et al. Usefulness of minimum clinically important difference for assessing patients with subaxial degenerative cervical spine disease: statistical versus substantial clinical benefit , 2013, Acta Neurochirurgica.
[22] M. Maurer,et al. THAOS – The Transthyretin Amyloidosis Outcomes Survey: initial report on clinical manifestations in patients with hereditary and wild-type transthyretin amyloidosis , 2013, Current medical research and opinion.
[23] P. Dyck,et al. Dissociated sensation in amylidosis. Compound action potential, quantitative histologic and teased-fiber, and electron microscopic studies of sural nerve biopsies. , 1969, Archives of neurology.