论文信息 - Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study. - 字舞流文

Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study.

B. Burton | M. Inbar‐Feigenberg | J. Muenzer | D. Whiteman | P. Harmatz | N. Guffon | M. Ruiz-García | D. Bratkovic | D. Alexanderian | L. Gutiérrez-Solana | Yuna Wu | Simon A Jones | K. Yee | M. Hale