Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients.
暂无分享,去创建一个
A. Zwinderman | M. Hayden | E. Aronica | J. Kastelein | E. Stroes | M. Levi | K. High | J. Kuivenhoven | J. Twisk | C. Ross | M. Nierman | R. Franssen | C. Henny | Marcel M. Levi | J. Meulenberg | M. Maas
[1] Marcela V Maus,et al. CD8+ T-cell responses to adeno-associated virus capsid in humans , 2007, Nature Medicine.
[2] M. Hayden,et al. Correction of feline lipoprotein lipase deficiency with adeno-associated virus serotype 1-mediated gene transfer of the lipoprotein lipase S447X beneficial mutation. , 2006, Human gene therapy.
[3] M. Hayden,et al. Gene therapy for lipoprotein lipase deficiency: working toward clinical application. , 2005, Human gene therapy.
[4] H. Venema,et al. Dixon Quantitative Chemical Shift MRI for Bone Marrow Evaluation in the Lumbar Spine: A Reproducibility Study in Healthy Volunteers , 2001, Journal of computer assisted tomography.