Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial
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P. Rancoita | L. Naldini | M. Roncarolo | F. Morena | S. Martino | C. Baldoli | A. Biffi | A. Quattrini | A. Aiuti | F. Ciceri | M. Sessa | F. Benedicenti | E. Montini | F. Fumagalli | D. Redaelli | M. Cicalese | A. Assanelli | M. Gabaldo | A. Calabria | U. Carro | R. Fiori | P. Silvani | Ignazio Lopez | S. Acquati | S. Canale | L. Lorioli | G. Antonioli | M. Sora | C. Serio | Sabrina Canale
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