论文信息 - Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study - 字舞流文

Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study

E. Mercuri | F. Muntoni | I. Desguerre | A. Kristensen | C. McDonald | L. Morgenroth | M. Tulinius | P. Trifillis | H. Gordish-Dressman | F. Buccella | A. N. Osorio | E. Henricson | Joel Jiang | Claudio L Santos | Jin Zhu