论文信息 - D01 Golodirsen induces exon skipping leading to sarcolemmal dystrophin expression in patients with genetic mutations amenable to exon 53 skipping - 字舞流文

D01 Golodirsen induces exon skipping leading to sarcolemmal dystrophin expression in patients with genetic mutations amenable to exon 53 skipping

E. Mercuri | F. Muntoni | L. Servais | L. Popplewell | G. Dickson | V. Straub | M. Guglieri | J. Domingos | M. Monforte | J. Morgan | A. Seferian | D. Frank | F. Schnell