Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA.
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A. Wenzel | W. Hauswirth | C. Kostic | Y. Arsenijévic | A. Bemelmans | Zhongyan Wang | F. Munier | J. Lem | M. Jaquet | D. Hornfeld | S. V. Crippa | D. Schorderet | S. Crippa | Y. Arsenijevic