CRISPR/Cas9-Induced (CTG⋅CAG)n Repeat Instability in the Myotonic Dystrophy Type 1 Locus: Implications for Therapeutic Genome Editing
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M. Willemse | B. Wieringa | V. Mouly | D. Furling | I. D. van Kessel | D. G. Wansink | S. Cumming | D. Monckton | G. Gourdon | W. J. van den Broek | Ellen L. van Agtmaal | L. M. André