论文信息 - Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector - 字舞流文

Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector

F. Monpoux | B. Neven | Manfred Schmidt | O. Hermine | Y. Beuzard | S. Blanche | F. Suarez | C. Kalle | F. Kuypers | M. Montalembert | E. Payen | P. Leboulch | C. Pondarré | J. Ribeil | R. Cavallesco | S. Chrétien | P. Bourget | S. Soni | M. Cavazzana | L. Sandler | F. Touzot | F. Lefrère | Salima Hacien-Bey-Abina