Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.
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William J Feuer | Edwin M Stone | Alexander Sumaroka | A. J. Roman | W. Hauswirth | T. Aleman | S. Kaushal | A. Cideciyan | S. Schwartz | T. Conlon | S. Boye | B. Byrne | S. Jacobson | W. Feuer | G. Fishman | E. Stone | E. Héon | A. Iannaccone | A. Sumaroka | J. Pang | R. Calcedo | Samuel G Jacobson | Tomas S Aleman | Artur V Cideciyan | Alejandro J Roman | Sharon B Schwartz | Elise Heon | William W Hauswirth | Gerald A Fishman | Barry J Byrne | Alessandro Iannaccone | Roberto Calcedo | Malgorzata Swider | Melani B. Olivares | Sanford L Boye | Ji-Jing Pang | Shalesh Kaushal | Thomas J Conlon | Ramakrishna Ratnakaram | Marc C Peden | Kirsten E Erger | Melani B Olivares | Cristina L Mullins | M. Peden | M. Świder | K. Erger | R. Ratnakaram | Cristina L. Mullins | Kirsten E. Erger
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