Long-Term Galsulfase Treatment Associated With Improved Survival of Patients With Mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome): 15-Year Follow-Up From the Survey Study
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R. Giugliani | P. Harmatz | N. Guffon | D. Ketteridge | C. Lampe | A. Quartel | Simon A. Jones | E. Leão‐Teles | Simon A Jones