Clinical and Molecular Disease Spectrum and Outcomes in Patients with Infantile-Onset Pompe Disease.
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M. Kabra | C. Rehder | S. Nampoothiri | D. Bali | P. Kishnani | N. Gupta | M. Muranjan | I. Verma | M. Kalaivani | R. Puri | Z. Kazi | Sujatha Jagdeesh