A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease.
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Wuh-Liang Hwu | Hanna Mandel | H. Mandel | W. Hwu | M. Nicolino | P. Kishnani | D. Corzo | Priya S Kishnani | Marc Nicolino | Florence Yong | Deyanira Corzo | Florence Yong
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