Improvement with ongoing Enzyme Replacement Therapy in advanced late-onset Pompe disease: a case study.
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D. Bali | D. Koeberl | P. Kishnani | L. Case | J. Mackey | S. Young | Stephanie M Dearmey
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D. Bali | D. Koeberl | P. Kishnani | L. Case | J. Mackey | S. Young | Stephanie M Dearmey