Enzyme replacement therapy for mucopolysaccharidosis VI: Growth and pubertal development in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase.
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P. Kaplan | R. Steiner | R. Giugliani | J. E. Wraith | B. Plecko | J. Hopwood | E. Teles | C. Whitley | P. Harmatz | N. Guffon | D. Ketteridge | M. Scarpa | M. Beck | I. Schwartz | S. Swiedler | C. Decker | Zi-Fan Yu | Laila Arash | M. C. Miranda | S. Conrad | M. C. S. Miranda | Zi‐Fan Yu