论文信息 - GS-14-ENVISION, a phase 3 study to evaluate efficacy and safety of givosiran, an investigational RNAi therapeutic targeting aminolevulinic acid synthase 1, in acute hepatic porphyria patients - 字舞流文

GS-14-ENVISION, a phase 3 study to evaluate efficacy and safety of givosiran, an investigational RNAi therapeutic targeting aminolevulinic acid synthase 1, in acute hepatic porphyria patients

H. Bonkovsky | P. Stein | L. Gouya | K. Anderson | D. Bissell | M. Balwani | P. Harper | B. Ritchie | D. D’Avola | J. Windyga | P. Aguilera | D. Rees | J. Langendonk | U. Stölzel | J. Phillips | P. Ventura | E. Sardh | A. Ivanova | A. Chan | C. Penz | A. Simon | C. Parker | Q. Dinh | S. Silver | G. Ross | Jiaan-Der Wang | Jeeyoung Oh | Y. Horie | P. Stewart | Gary Liu | Siobán B. Keel