L‐leucine improves anemia and growth in patients with transfusion‐dependent Diamond‐Blackfan anemia: Results from a multicenter pilot phase I/II study from the Diamond‐Blackfan Anemia Registry
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Jason E. Farrar | Ellen V. Muir | G. Nalepa | J. Lipton | B. Glader | A. Narla | A. Vlachos | C. Sieff | E. Atsidaftos | Z. Rogers | K. Walkovich | C. Knoll | H. Hartung | B. Gruner | T. Loew | A. Panigrahi | J. Bernstein | Waseem Alhushki | Mohammad Lutfi Lababidi | J. Farrar