论文信息 - SMA – THERAPY P.260 Onasemnogene abeparvovec gene therapy in presymptomatic spinal muscular atrophy (SMA): SPR1NT study update - 字舞流文

SMA – THERAPY P.260 Onasemnogene abeparvovec gene therapy in presymptomatic spinal muscular atrophy (SMA): SPR1NT study update

R. Finkel | K. Strauss | F. Muntoni | C. Zaidman | L. Servais | M. Schultz | S. Iannaccone | K. Swoboda | J. Kwon | P. Shieh | M. Farrar | C. Chiriboga | J. Parsons | M. Scoto | K. Saito | H. McMillan | J. Krueger | J. Mendell | S. Group | F. Ogrinc