论文信息 - A novel DMD IRES results in a functional N-truncated dystrophin, providing a potential route to therapy for patients with 5’ mutations - 字舞流文

A novel DMD IRES results in a functional N-truncated dystrophin, providing a potential route to therapy for patients with 5’ mutations

M. Uhlén | R. Weiss | D. Dunn | K. Flanigan | A. Ferlini | A. Vulin | S. Messina | S. Wilton | B. Maiti | L. Rodino‐Klapac | C. Al-Khalili Szigyarto | G. Vita | F. Gualandi | C. Passarelli | Daniel R Schoenberg | B. Bakthavachalu | Maria Sofia Falzarano | A. Findlay | K. Heller | N. Wein | Lin Yang | M. Howard | L. Rodino-Klapac