论文信息 - Long-term clinical effect and safety of sebelipase alfa in adults with lysosomal acid lipase deficiency - 字舞流文

Long-term clinical effect and safety of sebelipase alfa in adults with lysosomal acid lipase deficiency

C. Twelves | S. Eckert | E. Schneider | S. Boyadjiev | C. Whitley | A. Quinn | Reena Sharma | V. Valayannopoulos | V. Malinová | R. Tripuraneni | Bruce Kessler | C. Bourdon