论文信息 - G.O.17 Results of a phase 2 open-label study of ISIS-SMNRx in patients with infantile (Type 1) spinal muscular atrophy - 字舞流文

G.O.17 Results of a phase 2 open-label study of ISIS-SMNRx in patients with infantile (Type 1) spinal muscular atrophy

R. Finkel | C. Bennett | J. Montes | C. Chiriboga | J. Day | M. Yamashita | K. Bishop | K. Alexander | D. McGuire | J. Vasjar | D. Cook | S. Paulose | D. Norris | R. Cruz | K. Watson | D. Vivo | L. McMillian