A retrospective study of paroxysmal nocturnal hemoglobinuria in pediatric and adolescent patients.

[1]  Pierre-Yves Dumas,et al.  Impact of eculizumab treatment on paroxysmal nocturnal hemoglobinuria: a treatment versus no‐treatment study , 2016, American journal of hematology.

[2]  A. Trehan,et al.  Frequency of Paroxysmal Nocturnal Hemoglobinuria Clones by Multiparametric Flow Cytometry in Pediatric Aplastic Anemia Patients of Indian Ethnic Origin , 2016, Pediatric blood & cancer.

[3]  R. Ware,et al.  Different clinical characteristics of paroxysmal nocturnal hemoglobinuria in pediatric and adult patients , 2015, Haematologica.

[4]  J. Svahn,et al.  Diagnosis and management of acquired aplastic anemia in childhood. Guidelines from the Marrow Failure Study Group of the Pediatric Haemato-Oncology Italian Association (AIEOP). , 2015, Blood cells, molecules & diseases.

[5]  F. Ravandi,et al.  A Prospective Multicenter Study of Paroxysmal Nocturnal Hemoglobinuria Cells in Patients with Bone Marrow Failure , 2013, Cytometry. Part B, Clinical cytometry.

[6]  P. Hillmen,et al.  Thrombosis in paroxysmal nocturnal hemoglobinuria. , 2013, Blood.

[7]  D. Blaise,et al.  Allogeneic stem cell transplantation in paroxysmal nocturnal hemoglobinuria , 2012, Haematologica.

[8]  K. Curran,et al.  Paroxysmal nocturnal hemoglobinuria in pediatric patients , 2012, Pediatric blood & cancer.

[9]  A. Risitano.  PAROXYSMAL nocturnal hemoglobinuria. , 2012, Journal of the American Medical Association.

[10]  K. Sakamoto,et al.  Efficacy and safety of eculizumab in children and adolescents with paroxysmal nocturnal hemoglobinuria , 2011, Pediatric blood & cancer.

[11]  L. Luzzatto,et al.  Management of Paroxysmal Nocturnal Haemoglobinuria: a personal view , 2011, British journal of haematology.

[12]  E. Thiel,et al.  A randomized controlled study in patients with newly diagnosed severe aplastic anemia receiving antithymocyte globulin (ATG), cyclosporine, with or without G-CSF: a study of the SAA Working Party of the European Group for Blood and Marrow Transplantation. , 2011, Blood.

[13]  F. Craig,et al.  Guidelines for the diagnosis and monitoring of paroxysmal nocturnal hemoglobinuria and related disorders by flow cytometry , 2010, Cytometry. Part B, Clinical cytometry.

[14]  A. Risitano,et al.  Hematopoietic stem cell transplantation for paroxysmal nocturnal hemoglobinuria: long-term results of a retrospective study on behalf of the Gruppo Italiano Trapianto Midollo Osseo (GITMO) , 2010, Haematologica.

[15]  H. Pati,et al.  Paroxysmal nocturnal hemoglobinuria in childhood and adolescence-a retrospective analysis of 18 cases , 2008, Indian journal of pediatrics.

[16]  N. Young,et al.  Multicenter phase 3 study of the complement inhibitor eculizumab for the treatment of patients with paroxysmal nocturnal hemoglobinuria. , 2008, Blood.

[17]  N. Young,et al.  Effect of the complement inhibitor eculizumab on thromboembolism in patients with paroxysmal nocturnal hemoglobinuria. , 2007, Blood.

[18]  S. Richards,et al.  Recent developments in the understanding and management of paroxysmal nocturnal haemoglobinuria , 2007, British journal of haematology.

[19]  N. Young,et al.  The complement inhibitor eculizumab in paroxysmal nocturnal hemoglobinuria. , 2006, The New England journal of medicine.

[20]  Vineeta Gupta,et al.  Paroxysmal nocturnal hemoglobinuria in childhood: an uncommon presentation. , 2006, Indian journal of medical sciences.

[21]  Neal Young,et al.  Diagnosis and management of paroxysmal nocturnal hemoglobinuria. , 2005, Blood.

[22]  R. Tamminga,et al.  Childhood paroxysmal nocturnal haemoglobinuria (PNH), a report of 11 cases in the Netherlands , 2005, British journal of haematology.

[23]  S. Richards,et al.  Effect of eculizumab on hemolysis and transfusion requirements in patients with paroxysmal nocturnal hemoglobinuria. , 2004, The New England journal of medicine.

[24]  S. Richards,et al.  Primary prophylaxis with warfarin prevents thrombosis in paroxysmal nocturnal hemoglobinuria (PNH). , 2003, Blood.

[25]  R. Storb,et al.  Hematopoietic cell transplantation from related and unrelated donors after minimal conditioning as a curative treatment modality for severe paroxysmal nocturnal hemoglobinuria. , 2003, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[26]  R. Brodsky,et al.  Paroxysmal nocturnal hemoglobinuria arising from Fanconi anemia. , 2003, Journal of pediatric hematology/oncology.

[27]  I. Ibrahim,et al.  Screening for paroxysmal nocturnal hemoglobinuria (PNH) clone in Egyptian children with aplastic anemia. , 2002, Journal of tropical pediatrics.

[28]  L. Matis,et al.  Inhibition of complement activity by humanized anti-C5 antibody and single-chain Fv. , 1996, Molecular immunology.

[29]  J. Mary,et al.  Paroxysmal nocturnal haemoglobinuria: long-term follow-up and prognostic factors , 1996, The Lancet.

[30]  C. Wittwer,et al.  Syngeneic bone marrow transplantation without conditioning in a patient with paroxysmal nocturnal hemoglobinuria: in vivo evidence that the mutant stem cells have a survival advantage. , 1996, Blood.

[31]  Rong-Long Chen,et al.  Paroxysmal nocturnal hemoglobinuria presenting as moyamoya syndrome , 1996 .

[32]  C. Miller,et al.  Resolution of Budd‐Chiari syndrome following bone marrow transplantation for paroxysmal nocturnal haemoglobinuria , 1996, British journal of haematology.

[33]  S M Lewis,et al.  Natural history of paroxysmal nocturnal hemoglobinuria. , 1995, The New England journal of medicine.

[34]  A. Mowat,et al.  Paroxysmal nocturnal haemoglobinuria and Budd-Chiari syndrome. , 1995, Archives of disease in childhood.

[35]  R. Ware,et al.  Paroxysmal nocturnal hemoglobinuria with onset in childhood and adolescence. , 1991, The New England journal of medicine.

[36]  P. Sims,et al.  The complement-inhibitory activity of CD59 resides in its capacity to block incorporation of C9 into membrane C5b-9. , 1990, Journal of immunology.

[37]  V. Nussenzweig,et al.  Inhibition of complement activation on the surface of cells after incorporation of decay-accelerating factor (DAF) into their membranes , 1984, The Journal of experimental medicine.

[38]  B Starfield,et al.  Child health care in the United States: a comparison of pediatricians and general practitioners. , 1981, The New England journal of medicine.

[39]  Ross Wf.  Paroxysmal nocturnal hemoglobinuria--present status and future prospects. , 1980 .

[40]  L. Diamond,et al.  Paroxysmal nocturnal hemoglobinuria in childhood and adolescence. Clinical and erythrocyte metabolic studies in two cases. , 1967, Pediatrics.

[41]  C. Niemeyer,et al.  Stem cell transplantation for paroxysmal nocturnal haemoglobinuria in childhood. , 2002, British journal of haematology.

[42]  L. Luzzatto,et al.  7 Paroxysmal nocturnal haemoglobinuria , 1989 .

[43]  M. Kletzel,et al.  Paroxysmal nocturnal hemoglobinuria presenting as recurrent hemolytic uremic syndrome. , 1987, La Clinica pediatrica.