Allogeneic hematopoietic cell transplantation for primary immune deficiency diseases: current status and critical needs.

[1]  C. Dvorak,et al.  Megadose CD34(+) cell grafts improve recovery of T cell engraftment but not B cell immunity in patients with severe combined immunodeficiency disease undergoing haplocompatible nonmyeloablative transplantation. , 2008, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[2]  E. Petersdorf.  Optimal HLA matching in hematopoietic cell transplantation. , 2008, Current opinion in immunology.

[3]  R. Somech,et al.  Matched unrelated bone marrow transplant for T+ combined immunodeficiency , 2008, Bone Marrow Transplantation.

[4]  M. Colonna,et al.  Innate immunity to pathogens. , 2008, Current opinion in immunology.

[5]  L. Notarangelo,et al.  Clinical features, long-term follow-up and outcome of a large cohort of patients with Chronic Granulomatous Disease: an Italian multicenter study. , 2008, Clinical immunology.

[6]  A. Fischer,et al.  Long-term outcome following hematopoietic stem-cell transplantation in Wiskott-Aldrich syndrome: collaborative study of the European Society for Immunodeficiencies and European Group for Blood and Marrow Transplantation. , 2008, Blood.

[7]  C. Dvorak,et al.  Hematopoietic stem cell transplantation for primary immunodeficiency disease , 2008, Bone Marrow Transplantation.

[8]  L. Notarangelo,et al.  Long-term immune reconstitution and clinical outcome after stem cell transplantation for severe T-cell immunodeficiency. , 2007, The Journal of allergy and clinical immunology.

[9]  J. Puck.  Population-based newborn screening for severe combined immunodeficiency: steps toward implementation. , 2007, The Journal of allergy and clinical immunology.

[10]  A. Fischer,et al.  Long-term T-cell reconstitution after hematopoietic stem-cell transplantation in primary T-cell-immunodeficient patients is associated with myeloid chimerism and possibly the primary disease phenotype. , 2007, Blood.

[11]  S. Donfield,et al.  Effect of myeloablative bone marrow transplantation on growth in children with sickle cell anaemia: results of the multicenter study of haematopoietic cell transplantation for sickle cell anaemia , 2007, British journal of haematology.

[12]  H. Malech,et al.  Genetics, biology and clinical management of myeloid cell primary immune deficiencies: chronic granulomatous disease and leukocyte adhesion deficiency , 2007, Current opinion in hematology.

[13]  A. Fischer,et al.  CD34+ stem cell top‐ups without conditioning after initial haematopoietic stem cell transplantation for correction of incomplete haematopoietic and immunological recovery in severe congenital immunodeficiencies , 2006, British journal of haematology.

[14]  F. Bonilla.  Development of Population-Based Newborn Screening for Severe Combined Immunodeficiency , 2006, Pediatrics.

[15]  J. Falkenburg,et al.  Long-term follow-up of myeloablative allogeneic stem cell transplantation using Campath ‘in the bag’ as T-cell depletion: the Leiden experience , 2006, Bone Marrow Transplantation.

[16]  K. Ness,et al.  Visual, auditory, sensory, and motor impairments in long‐term survivors of hematopoietic stem cell transplantation performed in childhood , 2006, Cancer.

[17]  L. Notarangelo,et al.  Bone marrow transplantation for severe combined immune deficiency. , 2006, JAMA.

[18]  P. Veys,et al.  Improved survival after unrelated donor bone marrow transplantation in children with primary immunodeficiency using a reduced-intensity conditioning regimen. , 2005, Blood.

[19]  R. Buckley.  Molecular defects in human severe combined immunodeficiency and approaches to immune reconstitution. , 2004, Annual review of immunology.

[20]  E. Austin.  Cellular Therapy: New Frontiers in Transfusion Medicine , 2004 .

[21]  D. Wall,et al.  Umbilical Cord Blood Transplantation in Severe T-Cell Immunodeficiency Disorders: Two-Year Experience , 2000, Journal of Clinical Immunology.

[22]  W. Friedrich,et al.  Severe combined immunodeficiency: treatment by bone marrow transplantation in 15 infants using HLA-haploidentical donors , 1985, European Journal of Pediatrics.

[23]  J. Casanova,et al.  An international study examining therapeutic options used in treatment of Wiskott-Aldrich syndrome. , 2003, Clinical immunology.

[24]  K. Schwarz,et al.  Autoimmunity in Wiskott-Aldrich syndrome: risk factors, clinical features, and outcome in a single-center cohort of 55 patients. , 2003, Pediatrics.

[25]  A. Fischer,et al.  Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968–99 , 2003, The Lancet.

[26]  A. Fischer,et al.  Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: a survey of the European experience, 1985-2000. , 2002, Blood.

[27]  E. Salido,et al.  A Founder Mutation in Artemis, an SNM1-Like Protein, Causes SCID in Athabascan-Speaking Native Americans1 , 2002, The Journal of Immunology.

[28]  J. Puck,et al.  Hematopoietic stem cell transplantation for severe combined immunodeficiency in the neonatal period leads to superior thymic output and improved survival. , 2002, Blood.

[29]  D. Glidden,et al.  Target dose adjustment of busulfan in pediatric patients undergoing bone marrow transplantation , 2001, Bone Marrow Transplantation.

[30]  S Mackinnon,et al.  Establishment of complete and mixed donor chimerism after allogeneic lymphohematopoietic transplantation: recommendations from a workshop at the 2001 Tandem Meetings of the International Bone Marrow Transplant Registry and the American Society of Blood and Marrow Transplantation. , 2001, Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation.

[31]  S. Holland,et al.  Treatment of chronic granulomatous disease with nonmyeloablative conditioning and a T-cell-depleted hematopoietic allograft. , 2001, The New England journal of medicine.

[32]  J. V. Stone,et al.  Impact of donor type on outcome of bone marrow transplantation for Wiskott-Aldrich syndrome: collaborative study of the International Bone Marrow Transplant Registry and the National Marrow Donor Program. , 2001, Blood.

[33]  K Godfrey,et al.  In the bag. , 2000, Nursing times.

[34]  A. Thrasher,et al.  The Wiskott–Aldrich syndrome , 2000, Clinical and experimental immunology.

[35]  P. Parham.  Primary immunodeficiency disease , 2000 .

[36]  K. Weinberg,et al.  T cell depleted haploidentical bone marrow transplantation for the treatment of children with severe combined immunodeficiency. , 2000, Archivum immunologiae et therapiae experimentalis.

[37]  M. Viele,et al.  Autoimmune hemolytic anemia in patients with SCID after T cell-depleted BM and PBSC transplantation , 1999, Bone Marrow Transplantation.

[38]  J. Roberts,et al.  Hematopoietic stem-cell transplantation for the treatment of severe combined immunodeficiency. , 1999, The New England journal of medicine.

[39]  K. Sullivan,et al.  A multiinstitutional survey of the Wiskott-Aldrich syndrome. , 1994, The Journal of pediatrics.

[40]  D. Wara,et al.  Immune reconstitution in severe combined immunodeficiency disease after lectin-treated, T-cell-depleted haplocompatible bone marrow transplantation. , 1993, Blood.

[41]  B. Dupont,et al.  Transplantation for severe combined immunodeficiency with HLA-A,B,D,DR incompatible parental marrow cells fractionated by soybean agglutinin and sheep red blood cells. , 1983, Blood.

[42]  H. Fudenberg.  Pediatric allergy and clinical immunology: Edited by C. Collins-Williams. University of Toronto Press, Toronto, 4th Ed., 1973. $6.50 , 1974 .

[43]  R. Albertini,et al.  Bone-marrow transplantation in a patient with the Wiskott-Aldrich syndrome , 1969 .

[44]  R. Gatti,et al.  Immunological reconstitution of sex-linked lymphopenic immunological deficiency. , 1968, Lancet.