CDKL5 mutations may mimic Pitt-Hopkins syndrome phenotype.
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A. Pinto | Aurora Currò | A. Renieri | M. Zappella | M. Bruttini | M. Zollino | G. Marangi | Gabriella Doddato
[1] X. Bao,et al. Rett and Rett‐like syndrome: Expanding the genetic spectrum to KIF1A and GRIN1 gene , 2019, Molecular genetics & genomic medicine.
[2] E. Pestana-Knight,et al. Cyclin-Dependent Kinase-Like 5 Deficiency Disorder: Clinical Review. , 2019, Pediatric neurology.
[3] E. Pestana-Knight,et al. CDKL5 deficiency disorder: Relationship between genotype, epilepsy, cortical visual impairment, and development , 2019, Epilepsia.
[4] J. Armstrong,et al. The most recurrent monogenic disorders that overlap with the phenotype of Rett syndrome. , 2019, European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society.
[5] Carol J. Saunders,et al. Diagnosis and management in Pitt‐Hopkins syndrome: First international consensus statement , 2019, Clinical genetics.
[6] Amanda S. Lindy,et al. Diagnostic outcomes for genetic testing of 70 genes in 8565 patients with epilepsy and neurodevelopmental disorders , 2018, Epilepsia.
[7] A. Fatemi,et al. Monogenic disorders that mimic the phenotype of Rett syndrome , 2018, neurogenetics.
[8] I. Kameshita,et al. A novel CDKL5 mutation in a Japanese patient with atypical Rett syndrome. , 2016, Clinica chimica acta; international journal of clinical chemistry.
[9] J. Christodoulou,et al. Functional abilities in children and adults with the CDKL5 disorder , 2016, American journal of medical genetics. Part A.
[10] R. Hennekam,et al. Phenotype and natural history in 101 individuals with Pitt-Hopkins syndrome through an internet questionnaire system , 2016, Orphanet Journal of Rare Diseases.
[11] A. de Weerd,et al. Respiratory and sleep disorders in female children with atypical Rett syndrome caused by mutations in the CDKL5 gene , 2013, Developmental medicine and child neurology.
[12] Meredith Wilson,et al. The CDKL5 disorder is an independent clinical entity associated with early-onset encephalopathy , 2012, European Journal of Human Genetics.
[13] R. Hennekam,et al. Development, cognition, and behaviour in Pitt–Hopkins syndrome , 2012, Developmental medicine and child neurology.
[14] A. Clarke,et al. Transcription Factor 4 and Myocyte Enhancer Factor 2C mutations are not common causes of Rett syndrome , 2012, American journal of medical genetics. Part A.
[15] A. Hoischen,et al. Severe mental retardation with breathing abnormalities (Pitt-Hopkins syndrome) is caused by haploinsufficiency of the neuronal bHLH transcription factor TCF4. , 2007, Human molecular genetics.
[16] Nathalie Boddaert,et al. Mutations in TCF4, encoding a class I basic helix-loop-helix transcription factor, are responsible for Pitt-Hopkins syndrome, a severe epileptic encephalopathy associated with autonomic dysfunction. , 2007, American journal of human genetics.
[17] J. Tolmie,et al. CDKL5 mutations cause infantile spasms, early onset seizures, and severe mental retardation in female patients , 2006, Journal of Medical Genetics.
[18] N. Landsberger,et al. CDKL5 belongs to the same molecular pathway of MeCP2 and it is responsible for the early-onset seizure variant of Rett syndrome. , 2005, Human molecular genetics.
[19] J. Gécz,et al. Mutations of CDKL5 cause a severe neurodevelopmental disorder with infantile spasms and mental retardation. , 2004, American journal of human genetics.
[20] J. Gécz,et al. Mutations in the X-linked cyclin-dependent kinase-like 5 (CDKL5/STK9) gene are associated with severe neurodevelopmental retardation. , 2004, American journal of human genetics.
[21] D. Pitt,et al. A Syndrome of Mental Retardation, Wide Mouth and Intermittent Overbreathing , 1978, Australian paediatric journal.