Quality of life improvements following one year of setmelanotide in children and adult patients with Bardet–Biedl syndrome: phase 3 trial results
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A. Gnanasakthy | P. Beales | H. Dollfus | J. Argente | A. Haqq | Karine Clément | G. Martos-Moreno | E. Forsythe | U. Mallya | C. Chirila | R. Haws | B. Buckley
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