论文信息 - Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: a national French retrospective study - 字舞流文

Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: a national French retrospective study

P. Latour | T. Levade | A. Brassier | B. Chabrol | M. Vanier | D. Eyer | P. Broué | C. Sevin | S. Pichard | C. Cances | F. Labarthe | C. Freihuber | B. Héron | Bahia Dahmani-Rabehi