论文信息 - Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B - 字舞流文

Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B

A. Shaywitz | P. Fitzpatrick | S. Bunting | A. Bagri | C. O’Neill | J. Brown | Catherine Vitelli | A. Grover | R. Lawrence | J. Pinkstaff | Bryan K. Yip | Jon Vincelette | M. Aoyagi-Scharber | Andrew C. Melton | Melanie J. Lo | Terri M. Christianson | John Holtzinger | Danielle Crippen-Harmon | K. Webster | J. Wait | Sara Rigney | S. Bullens | B. Baridon | Lacey Nave | B. Crawford | J. Lebowitz | Pascale M. N. Tiger