论文信息 - Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector - 字舞流文

Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector

L. D’Antiga | G. Ronzitti | T. Kishimoto | A. Iaconcig | A. Muro | F. Mingozzi | P. Ilyinskii | E. Nicastro | S. Charles | F. Collaud | C. Guarnaccia | F. Boisgérault | M. S. Sola | J. Rouillon | G. Bortolussi | Giulia De Sabbata | P. Vidal