In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease
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Rajan Jain | K. Musunuru | P. Zoltick | Kshitiz Singh | H. A. Hartman | W. Peranteau | D. Frank | S. Bose | Apeksha Dave | Vishal Swaminathan | Haiying Li | Meghana V. Kashyap | F. D. De Bie | S. Jayachandran | P. Chandrasekaran | Brandon M White | P. Menon | Shiva Teerdhala | Tiankun Wang | Brandon M. White | A. Dave | Kshitiz Singh
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