EPI-743 reverses the progression of the pediatric mitochondrial disease--genetically defined Leigh Syndrome.
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E. Bertini | M. Klein | G. Pontrelli | D. Martinelli | C. Dionisi-Vici | M. Thoolen | A. Pastore | W. Shrader | S. Livadiotti | F. Piemonte | V. Kheifets | T. Corsetti | G. Tozzi | M. Catteruccia | Andrew Hinman | Guy Miller
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