Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease.
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Amna Z. Shah | R. Ali | Alexander J. Smith | Sophia-Martha kleine Holthaus | A. Rahim | S. Mole | J. Hoke | R. Maswood | M. Basche | S. Herranz-Martín | I. Klaska | Mikel Aristorena | G. Massaro | M. Hughes | O. Semenyuk
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