Newborn screening for Pompe disease in Italy: Long-term results and future challenges
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L. Salviati | A. Burlina | G. Polo | A. Burlina | Evelina Maines | Stijn L. M. in ’t Groen | V. Gragnaniello | D. Gueraldi | C. Cazzorla | G. di Salvo | P. Pijnappel | G. Di Salvo
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