Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice
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A. Annoni | L. Naldini | M. Roncarolo | M. Akbarpour | A. D’Angelo | P. Della Valle | Sara Bartolaccini | K. Goudy | F. Russo | Alessio Cantore | Mahzad Akbarpour