论文信息 - Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy. - 字舞流文

Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy.

J. Mendell | W. Arnold | T. Prior | J. Kissel | D. Feltner | L. Alfano | L. Lowes | S. Al-Zaidy | R. Shell | K. Church | S. Nagendran | D. Sproule | C. Wells | K. Lehman | M. McColly | M. Menier