Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015–2022): 2022 interim analysis
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F. Muntoni | I. Desguerre | A. Kristensen | C. McDonald | S. Johnson | L. Morgenroth | M. Tulinius | P. Trifillis | H. Gordish-Dressman | F. Buccella | J. Kirschner | A. N. Osorio | E. Henricson | C. Werner | Eugenio Mercuri | Maria Bernadete Dutra de Resende
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