Lack of germline transmission in male mice following a single intravenous administration of AAV5-hFVIII-SQ gene therapy
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Joshua Henshaw | C. O’Neill | C. Fonck | Jaydeep K. Srimani | Cheng-Chen Su | Jeremy Arens | Elli Koziol | Andrea Van Tuyl | Sundeep Chandra | C. Vettermann | J. Arens | A. Van Tuyl