Nedosiran in primary hyperoxaluria subtype 3: results from a phase I, single-dose study (PHYOX4)
暂无分享,去创建一个
J. Lieske | J. Groothoff | G. Schalk | Blaž Vrhnjak | Kerry Russell | David S. Goldfarb | Shuli Yu | Gesa Schalk
[1] F. Modersitzki,et al. Healthcare utilization, quality of life, and work productivity associated with primary hyperoxaluria: a cross-sectional web-based US survey , 2023, Urolithiasis.
[2] J. Lieske,et al. PHYOX2: A Pivotal Randomized Study of Nedosiran in Primary Hyperoxaluria Type 1 or 2. , 2022, Kidney international.
[3] M. Stoller,et al. Perspectives in primary hyperoxaluria — historical, current and future clinical interventions , 2021, Nature Reviews Urology.
[4] B. Hoppe,et al. Safety, pharmacodynamics, and exposure-response modeling results from a first in human phase 1 study of nedosiran in primary hyperoxaluria. , 2021, Kidney international.
[5] J. Lieske,et al. Primary Hyperoxaluria Type 3 Can Also Result in Kidney Failure: A Case Report. , 2021, American journal of kidney diseases : the official journal of the National Kidney Foundation.
[6] M. Zaniew,et al. A report from the European Hyperoxaluria Consortium (OxalEurope) Registry on a large cohort of patients with primary hyperoxaluria type 3. , 2021, Kidney international.
[7] J. Lieske,et al. Clinical characterization of primary hyperoxaluria type 3 in comparison to types 1 and 2: a retrospective cohort study. , 2021, Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association.
[8] W. Lowther,et al. Endpoints for Clinical Trials in Primary Hyperoxaluria. , 2020, Clinical journal of the American Society of Nephrology : CJASN.
[9] D. Wattenberg,et al. Primary Hyperoxaluria: The Patient and Caregiver Perspective. , 2020, Clinical journal of the American Society of Nephrology : CJASN.
[10] R. Holmes,et al. Reduction in urinary oxalate excretion in mouse models of Primary Hyperoxaluria by RNA interference inhibition of liver lactate dehydrogenase activity. , 2019, Biochimica et biophysica acta. Molecular basis of disease.
[11] Yanhan Li,et al. Mutation Hot Spot Region in the HOGA1 Gene Associated with Primary Hyperoxaluria Type 3 in the Chinese Population , 2019, Kidney and Blood Pressure Research.
[12] Guofeng Xu,et al. Nine novel HOGA1 gene mutations identified in primary hyperoxaluria type 3 and distinct clinical and biochemical characteristics in Chinese children , 2019, Pediatric Nephrology.
[13] B. Hoppe,et al. Metabolic profile and impact of diet in patients with primary hyperoxaluria , 2018, International Urology and Nephrology.
[14] E. Salido,et al. Specific Inhibition of Hepatic Lactate Dehydrogenase Reduces Oxalate Production in Mouse Models of Primary Hyperoxaluria , 2018, Molecular therapy : the journal of the American Society of Gene Therapy.
[15] Lisa E. Vaughan,et al. Predictors of Incident ESRD among Patients with Primary Hyperoxaluria Presenting Prior to Kidney Failure. , 2016, Clinical journal of the American Society of Nephrology : CJASN.
[16] J. Bacchetta,et al. Renal function can be impaired in children with primary hyperoxaluria type 3 , 2015, Pediatric Nephrology.
[17] J. Lieske,et al. Phenotype-Genotype Correlations and Estimated Carrier Frequencies of Primary Hyperoxaluria. , 2015, Journal of the American Society of Nephrology : JASN.
[18] B. Hoppe. An update on primary hyperoxaluria , 2012, Nature Reviews Nephrology.
[19] Susan L. Furth,et al. Improved equations estimating GFR in children with chronic kidney disease using an immunonephelometric determination of cystatin C , 2012, Kidney international.
[20] W. Haley,et al. Primary hyperoxaluria type III gene HOGA1 (formerly DHDPSL) as a possible risk factor for idiopathic calcium oxalate urolithiasis. , 2011, Clinical journal of the American Society of Nephrology : CJASN.
[21] C. Charon,et al. Mutations in DHDPSL are responsible for primary hyperoxaluria type III. , 2010, American journal of human genetics.
[22] L. Stevens,et al. Estimating GFR using the CKD Epidemiology Collaboration (CKD-EPI) creatinine equation: more accurate GFR estimates, lower CKD prevalence estimates, and better risk predictions. , 2010, American journal of kidney diseases : the official journal of the National Kidney Foundation.
[23] P. Cochat,et al. Primary hyperoxaluria. , 2013, The New England journal of medicine.