Lethality rescue and long-term amelioration of a citrullinemia type I mouse model by neonatal gene-targeting combined to SaCRISPR-Cas9
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L. Zentilin | G. Ronzitti | A. Iaconcig | A. Muro | F. Collaud | L. Moretti | C. Guarnaccia | A. Vicidomini | Michela Lisjak