论文信息 - Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study - 字舞流文

Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study

T. Fleming | P. Slasor | B. Burton | C. Hendriksz | R. Giugliani | Shuan-Pei Lin | D. Hughes | P. Harmatz | V. Valayannopoulos | M. Scarpa | E. Mengel | W. Dummer | D. Lounsbury | Simon A. Jones | Simon A Jones