Reversal of blindness in animal models of leber congenital amaurosis using optimized AAV2-mediated gene transfer.
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J. F. Wright | G. Acland | C. Zeiss | J. Bennett | L. Dell’Osso | J. Jacobs | D. Chung | B. Hauck | K. High | V. Arruda | Shangzhen Zhou | A. Maguire | F. Mingozzi | J. Bennicelli | O. Zelenaia | A. Komáromy | T. Rex | G. Qu | Daniel J. Hui | Zhangyong Wei