Three-year safety results of SAR422459 (EIAV-ABCA4) gene therapy in patients with ABCA4-associated Stargardt disease: An open-label dose-escalation phase I/IIa clinical trial, cohorts 1-5.
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David J. Wilson | Elvira N. Chegarnov | J. Sahel | B. Lujan | Dongseok Choi | S. Mohand-Said | A. Lauer | I. Audo | R. Weleber | P. Benoit | M. Pennesi | Laura R. Erker | Maria A. Parker | Paul Yang | P. Barale | T. Appelqvist | Ambar Faridi | C. Ku | T. Stout | P. Steinkamp | M. M. da Palma | Melissa Krahmer | K. Sestakauskas | Caroline Ségaut-Prévost | Sarah Ayelo-Scheer | A. Faridi