Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
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T. Daly | N. Muzyczka | M. Haskins | M. Sands | T. Okuyama | C. Vogler | Thomas M. Daly | C. Vogler | M. E. Haskins | M. S. Sands | Torayuki Okuyama | Nicholas Muzyczka