Neuronopathic Gaucher disease: dysregulated mRNAs and miRNAs in brain pathogenesis and effects of pharmacologic chaperone treatment in a mouse model.
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Ying Sun | Stuart L. Tinch | K. Setchell | M. Keddache | Ronghua Li | M. Pandey | G. Grabowski | B. Liou | Yanyan Peng | Venette Inskeep | Wujuan Zhang | Nupur Dasgupta | You-hai Xu