论文信息 - A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice. - 字舞流文

A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice.

F. Muntoni | I. Eperon | K. Anthony | Haiyan Zhou | S. Wilton | J. Morgan | N. Janghra | Rachel L. Dickinson | C. Mitrpant | L. Price